New gene promoters could improve treatments for neurological diseases
A recently developed system for switching on the activity of genes could improve treatments for a broad range of neurological diseases. Source link...
Tag : Gene Therapy
FDA OKs 1st Stem Cell Human Trial for COVID-19
The stem cells from the placenta used in this treatment are “natural killer” cells that guard a developing fetus or newborn from viruses in the...
Plant-based relatives of cholesterol could boost gene-infused nanoparticle delivery
Gene-infused nanoparticles used for combating disease work better when they include plant-based relatives of cholesterol because their shape and structure help the genes get where...
Gene therapy approach could pave the way for treatment of Stargardt disease
A leading Professor of Ophthalmology at the University of Oxford has shared the details of his research which could pave the way for a new...
New gene therapy improves vision in blind mice
Mice born blind have shown significant improvement in vision after undergoing a new gene therapy developed by a team of Japanese scientists. Source link...
Rejuvenate Bio secures license to commercialize gene therapy for treating age-related diseases in dogs
Rejuvenate Bio has secured a license to commercialize a gene therapy technology developed at the Wyss Institute to treat multiple age-related diseases in dogs, which...
SITESEEKER to be used for Otsuka’s therapeutics discovery programs
PhoreMost will deploy its in-house expertise and next-generation phenotypic screening platform, SITESEEKER, in disease-relevant pathways nominated by Otsuka. Source link...
Scientists discover a new way to combine coding languages into single "bilingual" molecule
The nucleic acids of DNA encode genetic information, while the amino acids of proteins contain the code to turn that information into structures and functions....
Gene Therapy Breakthrough Could Treat Kidney Diseases
A new study has rekindled the hope kidney diseases can be treated with gene therapy. Source link...
Study shows safety, long-term beneficial impact of gene therapy for patients with Hemophilia A
A breakthrough gene therapy treatment for Haemophilia A has been shown to offer long-term benefits that have already transformed the lives of 13 men in...
Study shows the feasibility of using gene therapy to treat chronic traumatic encephalopathy
A new study shows the feasibility of using gene therapy to treat the progressive neurodegenerative disorder chronic traumatic encephalopathy. Source link...
Study uncovers a previously unknown subtype of muscle stem cells
Scientists have discovered a new subtype of muscle stem cells. These cells have the ability to build and regenerate new muscles, making them interesting targets...
Neuroscientists develop new method for uniquely targeted gene therapy
Neuroscientists at Lund University in Sweden have developed a new technology that engineers the shell of a virus to deliver gene therapy to the exact...
Beverly Davidson, PhD, Elected to the National Academy of Medicine
Beverly L. Davidson, PhD, director of the Raymond G. Perelman Center for Cellular and Molecular Therapeutics at Children’s Hospital of Philadelphia, has been elected to...
Faster, cheaper, better: improved gene therapy tool production
The heart of modern therapy is increasingly personalized and targeted at specific cellular or genetic deficits. This requires gene therapy, in many cases. A new...
New gene therapy helps stroke patients develop new neurons
Ischemic stroke is a condition in which parts of the brain lose their blood supply, causing nerve damage. Once brain tissue suffers irreparable harm, the...
Nanocapsules packed with gene-editing tools could be promising platform for many gene therapies
New tools for editing genetic code offer hope for new treatments for inherited diseases, some cancers, and even stubborn viral infections. But the typical method...