Tag : Duchenne Muscular Dystrophy

Latest News

New drug provides hope for patients with Duchenne muscular dystrophy

Newsemia
The results from three clinical trials have shown that a new drug can successfully delay the progression of Duchenne muscular dystrophy. Source link...
Latest News

New discovery could improve therapies for Duchenne muscular dystrophy

Newsemia
A new multi-institution study spearheaded by researchers at Florida State University and the University of California, Los Angeles suggests a tiny protein could play a...
Latest News

Researchers develop new method to boost efficiency of CRISPR gene editing in DMD

Newsemia
Scientists have developed a method to boost the efficiency of CRISPR gene editing in Duchenne muscular dystrophy (DMD), according to a study that could have...
Latest News

Unique gene therapy approach paves new way to tackle rare, inherited diseases

Newsemia
Nonsense mutations are single-letter errors in the genetic code that prematurely halt the production of critical proteins. These unfinished proteins are unable to function normally,...
Latest News

Single CRISPR treatment can safely and stably correct genetic disease

Newsemia
Researchers at Duke University have shown that a single systemic treatment using CRISPR genome editing technology can safely and stably correct a genetic disease —...
Neurology

Urine exRNA may be source of biomarkers for muscular dystrophy

Newsemia
Massachusetts General Hospital researchers have found that extracellular RNA in urine may be a source of biomarkers for the two most common forms of muscular...
Neurology

Pfizer terminates clinical studies evaluating domagrozumab for treatment of Duchenne muscular dystrophy

Newsemia
Pfizer Inc. announced today that it is terminating two ongoing clinical studies evaluating domagrozumab (PF-06252616) for the treatment of Duchenne muscular dystrophy (DMD): a Phase...

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