Tag: CFTR

Latest News

 Vertex Announces Reimbursement of Cystic Fibrosis Medicines SYMDEKO® (tezacaftor/ivacaftor and ivacaftor) for Eligible Patients Ages 12 and Older, and ORKAMBI® (lumacaftor/ivacaftor) in Children Ages 2 to 5, With Certain CFTR Mutations in Australia

Newsemia
LONDON–(BUSINESS WIRE)–Vertex announced reimbursement of SYMDEKO for eligible patients ages 12 and older, and ORKAMBI for children ages 2 to 5 in Australia. Source link...
Gastroenterology

The effect of CFTR modulators on a cystic fibrosis patient presenting with recurrent pancreatitis in the absence of respiratory symptoms: a case report

Newsemia
Cystic fibrosis (CF) is a genetic disorder of the epithelial CFTR apical chloride channel resulting in multi-organ manifestations, including pancreatic exocrine secretion. In the pancreas,...
Pharma / Biotech

GLPG1837, a CFTR potentiator, in p.Gly551Asp (G551D)-CF patients: An open-label, single-arm, phase 2a study (SAPHIRA1).

Newsemia
Related Articles GLPG1837, a CFTR potentiator, in p.Gly551Asp (G551D)-CF patients: An open-label, single-arm, phase 2a study (SAPHIRA1). J Cyst Fibros. 2019 May 27;: Authors: Davies...
Latest News

Vertex Announces European Commission Approval for KALYDECO® (ivacaftor) to Treat Patients with Cystic Fibrosis Aged 12 to <24 months with Certain Mutations in the CFTR Gene

Newsemia
LONDON–(BUSINESS WIRE)–Vertex Pharmaceuticals (Europe) Limited today announced that the European Commission has granted approval of the label extension for KALYDECO® (ivacaftor) to include the treatment...
Latest News

Vertex Announces European Authorization for Third Cystic Fibrosis Medicine SYMKEVI® (tezacaftor/ivacaftor), to be used in combination with ivacaftor (KALYDECO®), for People with CF Aged 12 and Older with Certain Mutations in the CFTR gene

Newsemia
LONDON–(BUSINESS WIRE)–Vertex Pharmaceuticals (Europe) Limited, today announced that the European Commission has granted Marketing Authorization for SYMKEVI® (tezacaftor/ivacaftor) in a combination regimen with ivacaftor (KALYDECO®)...
Latest News

CFTR potentiation by VX-770 involves stabilization of the pre-hydrolytic, O1 state

Newsemia
Langron, E; Prins, S; Vergani, P; (2018) CFTR potentiation by VX-770 involves stabilization of the pre-hydrolytic, O1 state. British Journal of Pharmacology 10.1111/bph.14475 . (In...
Latest News

Vertex reçoit un avis favorable du CHMP pour le SYMKEVI® (tezacaftor/ivacaftor) pour les personnes atteintes d'une fibrose kystique âgées de 12 ans et plus avec certaines mutations du gène CFTR

Newsemia
LONDRES–(BUSINESS WIRE)–Vertex Pharmaceuticals (Europe) Limited, a annoncé aujourd’hui que le Comité des médicaments à usage humain (CHMP) de l’Agence européenne du médicament (EMA) a adopté...

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